Publication
Ataluren for the treatment of nonsense-mutation cystic fibrosis: a randomised, double-blind, placebo-controlled phase 3 trial
Eitan Kerem, Michael W Konstan, Kris De Boeck, Frank J Accurso, Isabelle Sermet-Gaudelus, Michael Wilschanski, J Stuart Elborn, Paola Melotti, Inez Bronsveld, Isabelle Fajac, Anne Malfroot, Daniel B Rosenbluth, Patricia A Walker, Susanna A McColley, Christiane Knoop, Serena Quattrucci, Ernst Rietschel, Pamela L Zeitlin, Jay Barth, Gary L Elfring, Ellen M Welch, Arthur Branstrom, Robert J Spiegel, Stuart W Peltz, Temitayo Ajayi, Steven M Rowe
The Lancet Respiratory Medicine, July 2014, Elsevier
DOI: 10.1016/s2213-2600(14)70100-6