Publication
Standardising clinical outcomes measures for adult clinical trials in Fabry disease: A global Delphi consensus
D. Moreno-Martinez, P. Aguiar, C. Auray-Blais, M. Beck, D.G. Bichet, A. Burlina, D. Cole, P. Elliott, U. Feldt-Rasmussen, S. Feriozzi, J. Fletcher, R. Giugliani, A. Jovanovic, C. Kampmann, M. Langeveld, O. Lidove, A. Linhart, M. Mauer, J.C. Moon, A. Muir, A. Nowak, J.P. Oliveira, A. Ortiz, G. Pintos-Morell, J. Politei, P. Rozenfeld, R. Schiffmann, E. Svarstad, A.S. Talbot, M. Thomas, C. Tøndel, D. Warnock, M.L. West, D.A. Hughes
Molecular Genetics and Metabolism, April 2021, Elsevier
DOI: 10.1016/j.ymgme.2021.02.001