Publication
Analysis of the baseline characteristics of Fabry disease patients screened for the pegunigalsidase alfa phase III BALANCE study
David Warnock, Wallace Eric, Raphael Schiffmann, Myrl Holida, Ozlem Goker-Alpan, Robert Hopkin, Pilar Giraldo, Nedd Khan, Bojan Vujkovac, William Wilcox, Ales Linhart, Camilla Tøndel, Bruce A. Barshop, Amel Karaa, Maria Judit Molnar, Patrick Deegan, Jerry Vockley, William Rhead, Virginia Kimonis, Raul Chertkoff, Nicola Longo
Molecular Genetics and Metabolism, February 2019, Elsevier
DOI: 10.1016/j.ymgme.2018.12.389