Publication
A randomized, multicenter, multinational, phase 3B, open-label, parallel-group study of agalsidase beta in treatment-naive male pediatric patients with Fabry disease without severe symptoms: Baseline demographics and clinical data
Frits Wijburg, Bernard Bénichou, Daniel G. Bichet, Gabriela Dostalova, Lorne Clarke, Alejandro Fainboim, Andreas Fellgiebel, Cassiano Forcelini, Kristina An Haack, Robert Hopkin, C. Ronald Scott, Suma Shankar, Anna Tylki-Szymanska, Camilla Tøndel, Uma Ramaswami
Molecular Genetics and Metabolism, February 2013, Elsevier
DOI: 10.1016/j.ymgme.2012.11.272